Eteplirsen (AVI-4658; Exondys 51) is an antisense oligonucleotide approved in 2016 by FDA to treat Duchenne muscular dystrophy (DMD). Exondys 51 is specifically indicated for patients who have a confirmed mutation of the dystrophin gene amenable to exon 51 skipping, which affects about 13 percent of the population with DMD.

纯度：≥98%

CAS：1173755-55-9